Neurodegenerative and Neurodevelopmental Diseases Research Fund

The UC Davis Gene Therapy Center's Neurodegenerative and Neurodevelopmental Diseases Research Fund fuels pioneering research to develop precision, gene-targeted therapies for rare and currently untreatable disorders like CDKL5 Deficiency Disorder, Rett Syndrome, CASK-related Intellectual Disability, ZC4H2 Associated Rare Disorders, SMC1A Related Developmental and Epileptic Disorder, Jordan's Syndrome, Syngap1-related Intellectual Disabilities, Pitt Hopkins Syndrome, CNKSR2 related disorder, Juvenile Huntington's disease, and ADNP syndrome.

Through cutting-edge tools like gene therapy, CRISPR, and stem cell-derived models, researchers are working collaboratively to restore brain function, accelerate clinical breakthroughs, and bring lifelong cures to children and families affected by devastating neurological conditions.